gene therapy

noun

: the insertion of usually genetically altered genes into cells especially to replace defective genes in the treatment of genetic disorders or to provide a specialized disease-fighting function

gene therapist noun

Examples of gene therapy in a Sentence

advances in the science of gene therapy

Recent Examples on the Web

Pitt-Hopkins and precision gene therapy Pitt-Hopkins syndrome is a rare genetic disorder caused by a mutation in the TCF4 gene, which controls proteins that dictate brain and nervous system development. —Noah Lyons, San Diego Union-Tribune, 1 Jan. 2026

In 2025, researchers demonstrated that gene therapy could restore hearing in people born with a specific form of hereditary deafness caused by mutations in the OTOF gene. —Kaif Shaikh, Interesting Engineering, 1 Jan. 2026

The drugs on the list included Leqembi, which is used to treat early Alzheimer’s disease, and Casgevy, a gene therapy for sickle cell disease. —Berkeley Lovelace Jr, NBC news, 25 Dec. 2025

As our research on gene therapy progressed, NIH Small Business grants contributed to our founding a company that raised US$200 million in investments and partnerships and created hundreds of new jobs in Houston. —Fred D. Ledley, The Conversation, 15 Dec. 2025

Word History

First Known Use

1970, in the meaning defined above

Rhymes for gene therapy

• brachytherapy
• chemotherapy
• cryotherapy
• hydrotherapy
• hypnotherapy
• monotherapy
• phototherapy
• psychotherapy
• sclerotherapy
• immunotherapy
• pharmacotherapy
• physiotherapy

Kids Definition

gene therapy

noun

: the insertion of a functioning gene into cells especially to replace a defective gene in the treatment of genetic disorders

Medical Definition

gene therapy

noun

: the insertion of usually genetically altered genes into cells especially to replace defective genes in the treatment of genetic disorders or to provide a specialized disease-fighting function (as the destruction of tumor cells)

gene therapist noun