gene therapy

noun

: the insertion of usually genetically altered genes into cells especially to replace defective genes in the treatment of genetic disorders or to provide a specialized disease-fighting function
gene therapist noun

Examples of gene therapy in a Sentence

advances in the science of gene therapy
Recent Examples on the Web
Examples are automatically compiled from online sources to show current usage. Read More Opinions expressed in the examples do not represent those of Merriam-Webster or its editors. Send us feedback.
The company is seeking to create a Duchenne gene therapy that is more effective and safer than Sarepta Therapeutics’ Elevidys, which has been hampered by safety concerns, particularly following the deaths of two recipients from liver failure. Jason Mast, STAT, 14 May 2026 Prasad also faced backlash earlier this year for his rejection of a Huntington’s disease gene therapy from uniQure, which claimed the FDA was requiring it to perform fake brain surgery to evaluate whether the treatment works. Annika Kim Constantino,angelica Peebles, CNBC, 12 May 2026 In March, biotech company uniQure said the agency asked for an additional clinical trial of an experimental gene therapy for the fatal neurodegenerative disorder Huntington’s disease, dashing hopes of patients and advocates who’d hoped for a faster path to approval. Sarah Owermohle, CNN Money, 8 May 2026 Earlier this year, the agency decided not to review an application for a gene therapy to treat Huntington’s disease developed by drugmaker UniQure. Monica Alba, NBC news, 8 May 2026 See All Example Sentences for gene therapy

Word History

First Known Use

1970, in the meaning defined above

Time Traveler
The first known use of gene therapy was in 1970

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Cite this Entry

“Gene therapy.” Merriam-Webster.com Dictionary, Merriam-Webster, https://www.merriam-webster.com/dictionary/gene%20therapy. Accessed 18 May. 2026.

Kids Definition

gene therapy

noun
: the insertion of a functioning gene into cells especially to replace a defective gene in the treatment of genetic disorders

Medical Definition

gene therapy

noun
: the insertion of usually genetically altered genes into cells especially to replace defective genes in the treatment of genetic disorders or to provide a specialized disease-fighting function (as the destruction of tumor cells)
gene therapist noun

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